// App-Quantinova.ai

534 : TALEN-mediated gene editing of keratinocyte stem cells for a novel ex vivo epidermolytic ichthyosis therapy

Researchers

Presenter

  • O. March

Principal Investigators

  • M. Aushev

  • U. Koller

  • J. Reichelt

Medical Centers

  • Newcastle University, Newcastle, UNITED KINGDOM

  • EH House, Salzburg, Austria

Locations

  • United Kingdom

  • Austria

Companies

  • N/A

Study Components

Therapeutic Area

  • Genetic Disorder

  • Dermatology

Disease

  • Bullous congenital ichthyosiform erythroderma

Biomarkers

  • N/A

Drug/Treatment

  • N/A

Outcome

  • N/A


Study Design

  • N/A

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • Final