// App-Quantinova.ai

: Late onset Pompe Disease: A rare cause of respiratory failure

Researchers

Presenter

  • Rajini Sudhir

Principal Investigators

  • Richard Russell

  • Aziz Masruq

Medical Centers

  • NHS, Leicester (Leicestershire), United Kingdom

Locations

  • United Kingdom

Companies

  • N/A

Study Components

Therapeutic Area

  • Genetic Disorder

  • Musculoskeletal

  • Endocrine/metabolic Diseases (ME)

Disease

  • Glycogen storage disease 2

  • Cap myopathy

Biomarkers

  • N/A

Drug/Treatment

  • Acarbose

Outcome

  • N/A


Study Design

  • N/A

Phase

  • N/A

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A