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OC 64.4 : Modeling gray platelet syndrome: longitudinal mouse studies and in vitro human iPSC-derived megakaryocytes to investigate clinical and cellular features

Researchers

Presenter

  • J. Collins

Principal Investigators

  • L. Mayer

  • A. Sickmann

  • H. Zhou

  • G. Hoffman

  • W. Erber

  • C. Ghevaert

  • W. Ouwehand

  • J. Guerrero

Medical Centers

  • University of Cambridge, Cambridge, United Kingdom

  • Leibniz-Institut f»r Analytische Wissenschaften _ ISAS _ e.V., Dortmund, Nordrhein-Westfalen, Germany

  • Leibniz-Institut f»r Analytische Wissenschaften _ ISAS _ e.V., Dortmund, Nordrhein-Westfalen, Germany

  • Zhejiang Hisun Pharmaceutical, Taizhou Zhejiang, Jiangsu, China (People's Republic)

  • University of Western Australia, Western Australia, Australia

  • Department of Haematology, University of Cambridge and NHS Blood and Transplant, NIHR BioResource, Cambridge University Hospitals NHS Foundation Trust, Cambridge Biomedical Campus, Cambridge, CB2 0PT, UK. Department of Haematology, University College London Hospitals, London, NW1 2BU, UK, Cambridge, England, United Kingdom

Locations

  • United Kingdom

  • Germany

  • China

  • Australia

Companies

  • N/A

Study Components

Therapeutic Area

  • Genetic Disorder

  • Blood/haematological Diseases

Disease

  • Gray platelet syndrome

Biomarkers

  • Glasgow prognostic score

Drug/Treatment

  • N/A

Outcome

  • N/A


Study Design

  • N/A

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A