// App-Quantinova.ai

OC 01.5 : Innate and Adaptive Immune Responses to Adeno-Associated Viral Gene Therapy in the Severe Hemophilia A Dog Model

Researchers

Presenter

  • P. Batty

Principal Investigators

  • A. Mo

  • B. Yates

  • A. Gonzalez

  • B. Handyside

  • L. Harpell

  • D. Hurlbut

  • A. Pender

  • L. Razon

  • A. Winterborn

  • S. Fong

  • D. Lillicrap

Medical Centers

  • Kings College London, London, United Kingdom

  • Queen's University, Kingston, Ontario, Canada.

  • BioMarin Pharmaceutical, USA, Novato, California, United States

  • Kingston Health Sciences Center, Canada, Kingston, Ontario, Canada

  • Department of Biomedical and Molecular Sciences, Queen's University, Kingston, Ontario, Canada

Locations

  • United Kingdom

  • Canada

  • United States

Companies

  • N/A

Study Components

Therapeutic Area

  • Blood/haematological Diseases

Disease

  • Hemophilia

Biomarkers

  • N/A

Drug/Treatment

  • FVIII

Outcome

  • N/A


Study Design

  • Adaptive

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A