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S260 : SAFETY AND EFFICACY OF VOXELOTOR IN PEDIATRIC PATIENTS WITH SICKLE CELL DISEASE AGED 4-11 YEARS

Researchers

Presenter

  • Jeremie Estepp

Principal Investigators

  • Ramasubramanian Kalpatthi

  • Gerald Woods

  • Sara Trompeter

  • Robert Liem

  • Kacie Sims

  • Adlette Inati

  • Baba Inusa

  • Andrew Campbell

  • Connie Piccone

  • Miguel Abboud

  • Kim Smith-Whitley

  • Sandra Dixon

  • Margaret Tonda

  • Carla Washington

  • Clark Brown

Medical Centers

  • American University of Beirut Medical Center, Riad El Solh, Beirut, Lebanon

  • University College Hospitals London NHS Foundation Trust, London, England, United Kingdom

  • Children's Hospital of Pittsburgh of University of Pittsburgh Medical Center, Pittsburgh, PA

  • BMT, CHildrens Mercy Hospital, Kansas City, MO, United States

  • Lebanese American University, Beirut and Nini Hospital, Tripoli, Lebanon

  • Guy's And St Thomas NHS Foundation Trust, London, United Kingdom

  • UH Rainbow Babies and Children’s Hospital,Cleveland,United States

  • The Childrenaaas Hospital of Philadelphia, Philadelphia, Pennsylvania, United States

  • Global Blood Therapeutics, South San Francisco, CA, United States.

  • Children’s National Medical Center Washington DC United States

  • Childrens Healthcare of Atlanta, Atlanta, GA, United States,

  • Ann & Robert H. Lurie Childrens Hospital of Chicago, Chicago, Illinois, United States

  • St. Jude Affiliate Clinic Baton Rouge,Baton Rouge,United States

  • St Jude Childrens Research Hospital, Memphis, TN, United States

Locations

  • Lebanon

  • United Kingdom

  • United States

Companies

  • N/A

Study Components

Therapeutic Area

  • Blood/haematological Diseases

Disease

  • Sickle cell anemia

Biomarkers

  • Stearoyl-CoA desaturase

Drug/Treatment

  • Hydroxyurea

Outcome

  • N/A

Study Design

  • N/A

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A

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