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Mohamad Mohty
Ibrahim Yakoub-Agha
Marta Lisa Battista
Didier Blaise
Elisabetta Calore
Vian Amber
Robert J. Ryan
Katia Perruccio
Institut Paoli Calmettes, Aix Marseille University, CNRS, INSERM, CRCM,Marseille,France
Rheumatology Clinic, University of Udine, Udine, Italy
Department of Pediatric Hematology-Oncology, Azienda Ospedale, Università di Padova,Padova,Italy
Clinical Development, Jazz Pharmaceuticals,Oxford,United Kingdom
CHU de Lille, Univ Lille, INSERM U1286, Infinite,Lille,France
Jazz Pharmaceuticals,Philadelphia, PA,Verenigde Staten
Mother and Child Health, Santa Maria della Misericordia Hospital,Perugia,Italy
France
Italy
United Kingdom
United States
N/A
Gastroenterology (GU)
Hepatic veno-occlusive disease with immunodeficiency
Hyperbilirubinemia
Hematocrit
Defibrotide
N/A
Observational
Multinational
Multicenteric
Prospective
NA
NCT03032016
N/A
N/A