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EP1238 : LATE-ONSET VENO-OCCLUSIVE DISEASE/SINUSOIDAL OBSTRUCTION SYNDROME (VOD/SOS) AFTER HEMATOPOIETIC CELL TRANSPLANTATION (HCT): OUTCOMES OF DEFIBROTIDE-TREATED PATIENTS FROM THE EBMT PASS REGISTRY STUDY

Researchers

Presenter

  • Mohamad Mohty

Principal Investigators

  • Ibrahim Yakoub-Agha

  • Marta Lisa Battista

  • Didier Blaise

  • Elisabetta Calore

  • Vian Amber

  • Robert J. Ryan

  • Katia Perruccio

Medical Centers

  • Institut Paoli Calmettes, Aix Marseille University, CNRS, INSERM, CRCM,Marseille,France

  • Rheumatology Clinic, University of Udine, Udine, Italy

  • Department of Pediatric Hematology-Oncology, Azienda Ospedale, Università di Padova,Padova,Italy

  • Clinical Development, Jazz Pharmaceuticals,Oxford,United Kingdom

  • CHU de Lille, Univ Lille, INSERM U1286, Infinite,Lille,France

  • Jazz Pharmaceuticals,Philadelphia, PA,Verenigde Staten

  • Mother and Child Health, Santa Maria della Misericordia Hospital,Perugia,Italy

Locations

  • France

  • Italy

  • United Kingdom

  • United States

Companies

  • N/A

Study Components

Therapeutic Area

  • Gastroenterology (GU)

Disease

  • Hepatic veno-occlusive disease with immunodeficiency

  • Hyperbilirubinemia

Biomarkers

  • Hematocrit

Drug/Treatment

  • Defibrotide

Outcome

  • N/A


Study Design

  • Observational

  • Multinational

  • Multicenteric

  • Prospective

Phase

  • NA

Study Id's

  • NCT03032016

Sponsors

  • N/A

Result

  • N/A