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Franco Locatelli
Janet L. Kwiatkowski
Mark C. Walters
John B. Porter
Suradej Hongeng
Evangelia Yannaki
Andreas E. Kulozik
Martin G. Sauer
Adrian J. Thrasher
Isabelle Thuret
Ashutosh Lal
Ruiting Guo
Weijian Liu
Richard A. Colvin
Alexis A. Thompson
University Clinic Heidelberg, Heidelberg, Germany
Hospital de la Timone, Marseille, France
Ann & Robert H. Lurie Childrens Hospital of Chicago, Chicago, Illinois, United States
Mahidol University and Ramathibodi Hospital, Bangkok, Thailand,
Bambino Gesu Childrens Hospital, Rome, Italy
Great Ormond Street Institute of Child Health, UCL, London, United Kingdom
University College London Hospitals NHS Trust, London, United Kingdom
Ann &
Pediatrics, Benioff Children's Hospital Oakland, Oakland, CA, United States,
Medizinische Hochschule Hannover, Hannover, Germany
George Papanicolaou Hospital, Thessaloniki, Greece
bluebird bio Inc, Cambridge, United States,
Perelman School of Medicine at the University of Pennsylvania, Philadelphia, PA
Radiology, Children's Hospital of Philadelphia, Philadelphia, United States
Northwestern University Feinberg School of Medicine, Chicago, Illinois, United States
Germany
France
United States
Thailand
Italy
United Kingdom
Greece
N/A
Blood/haematological Diseases
Thalassemia
Cluster of Differentiation 34
Filgrastim
Plerixafor
Busulfan
N/A
Pharmacokinetics
III
NCT02906202
NCT03207009
N/A
N/A