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Regis Peffault de Latour
Carlos M. de Castro
Jeffrey Szer
Kensuke Usuki
Peter Hillmen
Morag Griffin
Mohammed Al-Adhami
Crystal Chen
Hisakazu Nishimori
Ilene C. Weitz
Jane Anne Nohl Division of Hematology,Keck-USC School of Medicine,Los Angeles, CA,United States
Royal Melbourne Hospital, Melbourne, Australia
Department of Hematology, NTT Medical Center Tokyo, Tokyo, Japan
Duke University, Durham, North Carolina, United States
French Reference Center for Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria, Assistance Publique – Hôpitaux de Paris, Université de Paris, Paris, France
Department of Obstetrics and Gynecology, Tokai Univeresity Hospital, Kanagawa, Japan
Apellis Pharmaceuticals, Inc.,Waltham,United States
Department of Clinical Haematology,Peter MacCallum Cancer Centre &
United States
Australia
Japan
France
United Kingdom
N/A
Blood/haematological Diseases
Paroxysmal nocturnal hemoglobinuria
N/A
Eculizumab
N/A
Randomized
Open Label
III
NCT03500549
N/A
N/A