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P1485 : A MULTICENTER, RETROSPECTIVE STUDY ON REAL-WORLD EXPERIENCE OF PATIENTS WITH SICKLE CELL DISEASE TREATED WITH VOXELOTOR

Researchers

Presenter

  • Biree Andemariam

Principal Investigators

  • Modupe Idowu

  • Nirmish Shah

  • Richard Drachtman

  • Archana Sharma

  • Alexander Glaros

  • Maureen Achebe

  • Alecia Nero

  • Susanna Curtis

  • Caterina Minnitti

Medical Centers

  • Rutgers - Robert Wood Johnson Medical School, New Brunswick, New Jersey, United States

  • Duke University School of Medicine,Durham,Stati Uniti

  • UT Southwestern Medical Center, Dallas, Texas, United States

  • Rutgers- Robert Wood Johnson Medical School, Piscataway, NJ

  • Rutgers Robert Wood Johnson Medical School,New Brunswick,États-unis

  • Pathology,Brigham and Women's Hospital,Boston,Estados Unidos

  • New England Sickle Cell Institute at the University of Connecticut, Farmington, CT

  • Albert Einstein College of Medicine,Bronx,Verenigde Staten

  • Rutgers Robert Wood Johnson Medical School,New Brunswick,États-unis

  • Division of Pediatric Hematology/Oncology,Central Michigan University,Detroit,États-unis

  • Albert Einstein College of Medicine, Bronx, New York, United States

  • University of Texas Southwestern Medical Center,Dallas,États-unis

  • New England Sickle Cell Inst

  • Alb

  • Division of Pediatric Hematology/Oncology,Central Michigan University,Detroit,États-unis

  • The University of Texas Southwestern Medical Center, Dallas, TX

  • University of Texas Health Center, Houston, TX, United States,

  • University of Texas Health,Houston,Estados Unidos

  • New England Sickle Cell Institute at the University of Connecticut, Farmington, CT

  • Duk

  • Division of Pediatric Hematology

  • Duke University School of Medicine,Durham,Verenigde Staten

  • University of Texas Health,Houston,Vereinigte Staaten

  • Duke University, Durham, North Carolina, United States

  • Brigham and Womens Hospital, Boston, MA, United States

  • Albert Einstein College of Medicine,Bronx,Verenigde Staten

  • Rutgers - Robert Wood Johnson Medical School, New Brunswick, New Jersey, United States

  • University of Texas Health,Houston,Estados Unidos

  • Albert Einstein College of Medicine, Great Neck, NY

  • New England Sickle Cell Institute, University of Connecticut Health,Farmington,États-unis

  • New England Sickle Cell Institute, University of Connecticut Health,Farmington,États-unis

  • Brigham and Womens Hospital, Boston, MA, United States

  • Division of Pediatric Hematology/Oncology,Central Michigan University,Detroit,États-unis

  • Duke University School of Medicine,Durham,Verenigde Staten

  • Albert Einstein College of Medicine,Bronx,États-unis

  • Brigham and Womens Hospital, Boston, MA, United States

  • The University of Texas Southwestern Medical Center, Dallas, TX

  • UT Southwestern Medical Center, Dallas, Texas, United States

  • University of Texas Southwestern Medical Center,Dallas,États-unis

  • Uni

  • University of Texas Health,Houston,Vereinigte Staaten

  • Pathology,Brigham and Women's Hospital,Boston,Estados Unidos

  • Division of Pediatric Hematology/Oncology,Central Michigan University,Detroit,États-unis

  • Pathology,Brigham and Women's Hospital,Boston,Estados Unidos

  • Rutgers Robert Wood Johnson Medical School,New Brunswick,États-unis

  • University of Texas Health,Houston,Estados Unidos

  • Brigham and Womens Hospital, Boston, MA, United States

  • Albert Einstein College of Medicine,Bronx,États-unis

  • Duke University School of Medicine,Durham,Stati Uniti

Locations

  • United States

  • United Kingdom

Companies

  • N/A

Study Components

Therapeutic Area

  • Blood/haematological Diseases

Disease

  • Sickle cell anemia

Biomarkers

  • Stearoyl-CoA desaturase

Drug/Treatment

  • Hydroxycarbamide

Outcome

  • N/A


Study Design

  • Multicenteric

Phase

  • N/A

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A