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: Enhancing FVIII Expression By Modifying B-Domain Sequence for Hemophilia A Gene Therapy

Researchers

Presenter

  • Doyoung Lee

Principal Investigators

  • Jenny McIntosh

  • Allison Dane

  • Cecilia Rosales

  • Anne Riddell

  • Edward Tuddenham

  • Amit C Nathwani

Medical Centers

  • Department of Haematology, UCL Cancer Institute, London, United Kingdom

  • Freeline, Stevenage, England, United Kingdom

  • Katharine Dormandy Haemophilia Centre and Thrombosis Unit, Royal Free NHS Trust, London, United Kingdom

Locations

  • United Kingdom

Companies

  • N/A

Study Components

Therapeutic Area

  • Blood/haematological Diseases

Disease

  • Hemophilia

Biomarkers

  • Cytochrome P450 Family 3 Subfamily A Member 4

Drug/Treatment

  • FVIII

Outcome

  • N/A


Study Design

  • N/A

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A