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: Alternative Donor Hematopoietic Stem Cell Transplantation for Sickle Cell Disease in Europe

Researchers

Presenter

  • Barbara Cappelli

Principal Investigators

  • Fernanda Volt

  • Selim Corbacioglu

  • Josu de la Fuente

  • Nathalie Dhedin

  • Corinne Pondarr

  • Juergen Foell

  • Farah O' Boyle

  • Arjan Lankester

  • Elisabetta Calore

  • Stefania Varotto

  • Marco Zecca

  • Amal Al-Seraihy

  • Mahmoud Aljurf

  • Anders Fasth

  • Sonia Bonanomi

  • Maria Carmen Addari

  • Franco Locatelli

  • Alina Ferster

  • Veerle Labarque

  • Peter Bader

  • Belinda Pinto Simes

  • Karina Tozatto-Maio

  • Vanderson Rocha

  • Mathieu Kuentz

  • Hanadi Elayoubi

  • Annalisa Ruggeri

  • Francoise Bernaudin

  • Eliane Gluckman

Medical Centers

  • Eurocord, Hopital Saint Louis APHP, University Paris-Diderot, Paris, France,

  • Centre Scientifique de Monaco, Monaco, Monaco

  • Internal Medicine III, Department of Hematology, Oncology and Stem Cell Transplantation, University Hospital Regensburg, Regensburg, Germany

  • Paediatrics, St Mary's Hospital, London, United Kingdom

  • Dermatology Department, Saint Louis Hospital, Paris, France

  • Pediatrics, Reference Center for Sickle Cell Disease, CHIC Hospital, Creteil, France

  • Internal Medicine III, Department of Hematology, Oncology and Stem Cell Transplantation, University Hospital Regensburg, Regensburg, Germany

  • Department of Orthopaedics, St George's Hospital, London, United Kingdom

  • Leiden University Medical Centre, Leiden, Netherlands

  • Pediatric Hematology-Oncology Unit, Department of Women's and Children's Health, Azienda Ospedaliera-University of Padova, Padova, Italy

  • Clinica di Emato-Oncologia Pediatrica, Azienda Ospedaliero-Universitaria di Padova, Padova, Italy

  • Medical Oncology, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy

  • Pedaitric Rheumatology, King Faisal Specialist Hospital & Research Center, Riyadh, Saudi Arabia

  • Oncology Center, King Faisal Specialist Hospital & Research Center, Riyadh, Saudi Arabia

  • Department of Paediatrics, University of Gothenburg and Queen Silvia Children's Hospital, Gothenburg, Sweden

  • Pediatric Clinic - Hemato-Oncology Department, University of Milano-Bicocca, MBBM Fundation c/o San Gerardo Hospital, Monza, Italy

  • Centro trapianti di midollo, Centro Microcitemie, Cagliari, Italy

  • Department of Pediatric Hematology and Oncology , IRCCS Ospedale Bambino Gesu, Rome , Italy

  • Université Libre de Bruxelles, Hematology-Oncology Unit, Hôpital Universitaire des Enfants Reine Fabiola, Brussels, Belgium

  • Department of Hematology, University Hospital Leuven, Leuven, Belgium

  • Hospital for Children and Adolescents; Division for Stem Cell Transplantation and Immunology, University Hospital Frankfurt, Frankfurt, Germany

  • Faculdade de Medicina de Ribeirao Preto - Universidade de Sao Paulo, Ribeirao Preto, Brazil

  • Bone Marrow Transplant Unit, Hospital Sirio Libanes, São Paulo, Brazil

Locations

  • France

  • Monaco

  • Germany

  • United Kingdom

  • Netherlands

  • Italy

  • Saudi Arabia

  • Sweden

  • Belgium

  • Brazil

Companies

  • N/A

Study Components

Therapeutic Area

  • Blood/haematological Diseases

  • Pulmonary/Respiratory Diseases

  • Autoimmune (AI)

Disease

  • Graft-versus-host disease

  • Acute chest syndrome

  • Sickle cell anemia

Biomarkers

  • Granulocyte colony-stimulating factor

  • Stearoyl-CoA desaturase

  • Red Blood Cells

Drug/Treatment

  • Mycophenolate mofetil

  • CKD-4101

  • Cyclophosphamide

  • Cyclophosphamide Injection

  • Cyclosporine A

  • Mycophenolic acid

  • Cyclosporine eent

  • Methotrexate

  • fludarabine tablet

  • Hydroxyurea

  • Hydroxycarbamide

  • Ovastat

  • Rapacan

  • Thiotepa

  • Alemtuzumab

  • Filgrastim

Outcome

  • N/A


Study Design

  • N/A

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A