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: A New Flow-Based Assay to Assess Treatment Response in Congenital Thrombotic Thrombocytopenic Purpura

Researchers

Presenter

  • Ferras Alwan

Principal Investigators

  • Chiara Vendramin

  • Alice Taylor

  • Mari Thomas

  • Ri Liesner

  • Marie Scully

Medical Centers

  • Department of Medical Oncology, University College London Hospital, London, United Kingdom

  • Haemostasis Research Unit, University College London, London, United Kingdom

  • Haemophilia Comprehensive Care Centre, Great Ormond Street Hospital for Children, London, United Kingdom

  • University College London (UCL) Hospitals/UCL Biomedical Research Centre, National Institute for Health Research Cardiometabolic Programme, London, United Kingdom

Locations

  • United Kingdom

Companies

  • N/A

Study Components

Therapeutic Area

  • Blood/haematological Diseases

  • Genetic Disorder

Disease

  • Thrombotic thrombocytopenic purpura

Biomarkers

  • von Willebrand factor

Drug/Treatment

  • thrombospondin-1

  • Aspirin

  • Albyl-E

Outcome

  • N/A


Study Design

  • N/A

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A