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T. Knudsen
P. B. Johansen
F. Del Greco
L. Neuman
H. Levy
J. Reckless
G. E. Blouse
Crescendo Bioscience, South San Francisco, United States
RxCelerate, Cambridge, United Kingdom
United States
United Kingdom
N/A
Genetic Disorder
Musculoskeletal
Hemophilia
Short stature, onychodysplasia, facial dysmorphism, and hypotrichosis
N/A
CB-813
N/A
N/A
III
N/A
N/A
N/A