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Regis Peffault De Latour
Jeffrey Szer
Austin G Kulasekararaj
Jin Seok Kim
Caroline I. Piatek
Alexander D. Kulagin
Anita Hill
Jimmy Wang
Ji Yu
Masayo Ogawa
Hubert Schrezenmeier
Jong Wook Lee
SBIM, Hopital Saint-Louis, APHP, Paris, France
Department of Medical Oncology, Royal Melbourne Hospital, Melbourne, Australia
King’s College Hospital, National Institute of Health Research/Wellcome King’s Clinical Research Facility and King’s College London,London,United Kingdom
Division of Cardiology, Department of Internal Medicine, Sevarance Hospital, Yonsei University College of Medicine, Seoul, Korea, Republic of
Division of Hematology, Keck School of Medicine, University of Southern California, Los Angeles, CA
RM Gorbacheva Research Institute, Pavlov University,St Petersburg,Russia
Vertex Pharmaceuticals Inc., Boston, MA
Vertex Pharmaceuticals Inc., Boston, MA
Institute of Transfusion Medicine, University of Ulm, and Institute for Clinical Transfusion Medicine and Immunogenetics, German Red Cross Blood Transfusion Service Baden-Württemberg-Hessen and University Hospital Ulm,Ulm,Germany
Seoul St. Mary's Hospital, College of Medicine, The Catholic University of Korea, Seoul, Korea
France
Australia
United Kingdom
Republic of South Korea
United States
Russia
Germany
N/A
Blood/haematological Diseases
Paroxysmal nocturnal hemoglobinuria
N/A
Eculizumab
N/A
Randomized
III
NCT02946463
NCT03056040
N/A
N/A