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Peter Hillmen
Jeffrey Szer
Ilene C. Weitz
Alexander Rth
Britta Hoechsmann
Jens Panse
Kensuke Usuki
Morag Griffin
Jean-Jacques Kiladjian
Carlos M. de Castro
Hisakazu Nishimori
Lisa Tan
Mohamed Hamdani
Pascal Deschatelets
Cedric Francois
Federico Grossi
Antonio Risitano
Regis Peffault De Latour
Department of Diabetes and Endocrinology, St James University Hospital, Leeds, United Kingdom
Department of Medical Oncology, Royal Melbourne Hospital, Melbourne, Australia
Jane Anne Nohl Division of Hematology, Keck School Of Medicine of USC, Los Angeles, CA
Department of Dermatology, University Hospital, University Duisburg-Essen, Essen, Germany
University of Ulm and Institute of Clinical Transfusion Medicine and Immunogenetics,German Red Cross Blood Transfusion Service and University Hospital Ulm, Institute of Transfusion Medicine,Ulm,Germany
Department of Oncology, Hematology and Stem Cell Transplantation, University Hospital of the RWTH Aachen, Aachen, Germany
Department of Hematology, NTT Medical Center Tokyo, Tokyo, Japan
Centre d'Investigations Cliniques, Hôpital Saint-Louis; Assistance Publique – Hôpitaux de Paris; Université de Paris, Paris, France
Duke University College of Medicine, Durham, NC
Department of Gastroenterology, Kanazawa University Hospital, Ishikawa, Japan
Lisa Tan Pharma Consulting, Cambridge, United Kingdom
AMAG Pharmaceuticals, Inc., Waltham, MA
Department of Clinical Medicine and Surgery, Federico II University, Naples, Italy
French Reference Center for Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria, Assistance Publique – Hôpitaux de Paris, Université de Paris, Paris, France
United Kingdom
Australia
United States
Germany
Japan
France
Italy
N/A
Blood/haematological Diseases
Paroxysmal nocturnal hemoglobinuria
Lactate dehydrogenase
Eculizumab
N/A
Randomized
Superiority
III
NCT03500549
N/A
N/A