//
Maria Domenica Cappellini
Ali T. Taher
Antonio Piga
Farrukh Shah
Ersi Voskaridou
Vip Viprakasit
John B. Porter
Olivier Hermine
Ellis J. Neufeld
Alexis A. Thompson
Derek Tang
Peiwen Yu
Shien Guo
Jeevan K. Shetty
Dimana Miteva
Tatiana Zinger
Jay T. Backstrom
Esther Natalie Oliva
University of Milan, Milan, Italy
Department of Pediatrics and Adolescent Medicine, American University of Beirut Medical Center, Beirut, Lebanon
Dept of Clinical and Biological Sciences, University of Turin, Turin, Italy
Department of Microbiology, Whittington Health NHS Trust, London, United Kingdom
Thalassemia and Sickle Cell Center ,Laiko General Hospital,Athens,Grecia
Ramathibodi Hospital, Mahidol University, Bangkok, Thailand
University College London Hospitals NHS Trust, London, United Kingdom
Necker Hospital, Assistance Publique-Hopitaux de Paris, Paris, France
Imagine Institute, INSERM U1163, University of Paris, Paris, France
St. Jude Children's Research Hospital, Memphis, TN
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, IL
Bristol-Myers Sqiubb, Princeton, NJ
Evidera, Waltham, MA
Acceleron Pharma, Cambridge, MA
Grande Ospedale Metropolitano Bianchi-Melacrino-Morelli, Reggio Calabria, Italy
Italy
Lebanon
United Kingdom
Greece
Thailand
France
United States
N/A
Genetic Disorder
Ophthalmology (OP)
Beta-thalassemia
Solute Carrier Family 12 Member 2
luspatercept
N/A
N/A
III
NCT02604433
N/A
N/A