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Franco Locatelli
Maura Faraci
Ibrahim Yakoub-Agha
Stephane Girault
Kate Wheeler
Robert J. Ryan
Raj Hanvesakul
Mohamad Mohty
Department of Pediatric Hematology and Oncology,IRCCS Bambino Gesù Children's Hospital, Sapienza University of Rome,Rome,Italie
Istituto Giannina Gaslini, Genoa, Italy
CHU de Lille, Univ Lille, INSERM U1286, Infinite,Lille,France
Hematologie Clinique et Therapie Cellulaire, Limoges, France
Paediatric Oncology, Oxford Children’s Hospital, Oxford, United Kingdom
Merck Pharmaceuticals, Philadelphia, PA
Jazz Pharmaceuticals,Oxford,United Kingdom
Hôpital St Antoine, Sorbonne University, INSERM UMRs 938, Paris, France
Italy
France
United Kingdom
United States
N/A
Infectious Diseases (ID)
Hepatic veno-occlusive disease with immunodeficiency
Gastrointestinal bleeding
Hyperbilirubinemia
Sepsis
N/A
Defibrotide
N/A
Observational
Multinational
Multicenteric
Prospective
NA
NCT03032016
N/A
N/A