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776 : Improvement in Erythropoiesis Following Treatment with Betibeglogene Autotemcel Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia in the Phase 3 Hgb-207 Study

Researchers

Presenter

  • John B. Porter

Principal Investigators

  • Alexis A. Thompson

  • Mark C. Walters

  • Janet L. Kwiatkowski

  • Suradej Hongeng

  • Martin G. Sauer

  • Adrian J. Thrasher

  • Isabelle Thuret

  • Ruiting Guo

  • Richard A. Colvin

  • Franco Locatelli

Medical Centers

  • Department of Medical Oncology, University College London Hospital, London, United Kingdom

  • Pediatrics/Hematology, Oncology & Stem Cell Transplant, Northwestern University Feinberg School of Medicine, Chicago, IL

  • Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, IL

  • UCSF Benioff Childrens Hospital Oakland, Oakland, CA

  • Department of Pathology, The Children's Hospital of Philadelphia, Philadelphia, PA

  • Division of Hematology/Oncology, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, PA

  • Mahidol University and Ramathibodi Hospital, Bangkok, Thailand,

  • Dept. of Hematology/Oncology, Medizinische Hochschule Hannover, Hannover, Germany

  • Great Ormond Street Institute of Child Health, UCL, London, United Kingdom

  • Pediatric Hematology Department, Hopital de La Timone, Marseille, France

  • bluebird bio, Inc., Cambridge, MA.

  • Department of Pediatric Hematology and Oncology, Cell and Gene Therapy,IRCCS Bambino Gesù Children's Hospital,Roma,Italy

Locations

  • United Kingdom

  • United States

  • Thailand

  • Germany

  • France

  • Italy

Companies

  • N/A

Study Components

Therapeutic Area

  • Blood/haematological Diseases

Disease

  • Transfusion-dependent β-thalassemia

Biomarkers

  • Cluster of Differentiation 34

  • Granulocyte colony-stimulating factor

Drug/Treatment

  • Plerixafor

  • Busulfan

  • Filgrastim

Outcome

  • N/A

Study Design

  • Pharmacokinetics

Phase

  • III

Study Id's

  • NCT02906202

Sponsors

  • N/A

Result

  • N/A

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