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Thomas Meier
Christian Rummey
Mika Leinonen
Shabir Hasham
Thomas Voit
Oscar H Mayer
Gunnar M Buyse
Santhera Pharmaceuicals, Pratteln, Switzerland
Great Ormond Street Institute of Child Health, UCL, London, United Kingdom
Children's Hospital of Philadelphia, Philadelphia, United States of America
Switzerland
United Kingdom
United States
Belgium
N/A
Genetic Disorder
Musculoskeletal
Duchenne muscular dystrophy
N/A
Glucocorticoid
Idebenone
Roxithromycin
N/A
Randomized
Placebo Control
Controlled
III
N/A
N/A
N/A