//
Christopher Denton
N/A
Department of Rheumatology, University College London, London, UK
United Kingdom
N/A
Genetic Disorder
Central Nervous System (CNS)
Scleroderma
Mental retardation, X-linked, syndromic, 15
N/A
Mycophenolate mofetil
CKD-4101
Cyclophosphamide
Cyclophosphamide Injection
Mycophenolic acid
Methotrexate
Tocilizumab
Abatacept
N/A
Placebo Control
Superiority
Observational
NA
N/A
N/A
N/A