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: Antisense oligonucleotide treatment in CEP290‐related leber congenital amaurosis

Researchers

Presenter

  • Bart P Leroy

Principal Investigators

  • Artur V Cideciyan

  • Samuel G Jacobson

  • Arlene V Drack

  • Allen C Ho

  • Alexandra Garafalo

  • Alejandro J Roman

  • Mike Schwartz

  • Patricia Biasutto

  • Wilma de Wit

  • Michael E Cheetham

  • Peter S Adamson

  • David Rodham

  • Aniz Girach

  • Julie De Zaeytijd

  • Caroline Van Cauwenbergh

  • Stephen R Russell

Medical Centers

  • Department of Ophthalmology & Center for Medical Genetics, Ghent University Hospital & Ghent University, Ghent, Belgium

  • Scheie Eye Institute, University of Pennsylvania, Philadelphia, USA

  • Ophthalmology and Visual Sciences, University of Iowa, Coralville, Iowa, United States

  • Wills Eye Hospital, Thomas Jefferson University, Philadelphia, PA, USA

  • ProQR Therapeutics NV, Leiden, Netherlands

  • UCL, Institute of Ophthalmology, London, United Kingdom

  • Department of Surgery, Ghent University Hospital, Ghent, Belgium

Locations

  • Belgium

  • United States

  • Netherlands

  • United Kingdom

Companies

  • N/A

Study Components

Therapeutic Area

  • Ophthalmology (OP)

  • Congenital disorder

Disease

  • Leber congenital amaurosis

Biomarkers

  • N/A

Drug/Treatment

  • N/A

Outcome

  • N/A

Study Design

  • N/A

Phase

  • NA

Study Id's

  • NCT03140969

Sponsors

  • N/A

Result

  • N/A

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