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PO‐109 : Management of congenital thrombotic thrombocytopenic purpura using BPL Factor 8Y; a single centre report

Researchers

Presenter

  • A Akinsete

Principal Investigators

  • M Williams

  • J Motwani

Medical Centers

  • Haematology, Birmingham Children's Hospital, Birmingham, UK

  • Department of Haematology, Birmingham Childrens Hospital, Birmingham, United Kingdom

Locations

  • United Kingdom

Companies

  • N/A

Study Components

Therapeutic Area

  • Blood/haematological Diseases

Disease

  • N/A

Biomarkers

  • ZFP36 Ring Finger Protein Like 1

Drug/Treatment

  • FVIII

Outcome

  • N/A


Study Design

  • Single Center

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A