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G. Young
R. Liesner
R. Sidonio
J. Oldenburg
V. Jimenez-Yuste
J. Malangu
R. Kruse-Jarres
M. Wang
T. Chang
M. Uguen
M. Doral
C. Schmitt
G. Levy
M. Shima
M.E. Mancuso
Childrens Hospital Los Angeles, University of Southern California Keck School of Medicine, Los Angeles, CA
Great Ormond Street Hospital, London, United Kingdom
Emory University and Children's Healthcare of Atlanta, Atlanta, GA
University Hospital Bonn, Bonn, Germany
La Paz University Hospital, Madrid, Spain
University of Witwatersrand, Johannesburg, South Africa
Bloodworks Northwest, Seattle, WA
Univeristy of Colorado, Denver, CO
Genentech Inc., San Francisco, United States
F. Hoffmann-La Roche Ltd., Basel, Switzerland
Nara Medical University, Kashihara, Japan
Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy
United States
United Kingdom
Germany
Spain
South Africa
Switzerland
Japan
Italy
N/A
Musculoskeletal
Blood/haematological Diseases
Thrombotic microangiopathy
Hemophilia
N/A
FVIII
N/A
Pharmacokinetics
Prospective
Cohort
NA
NCT02795767
NCT02476942
Roche Holding AG and Chugai Pharmaceutical Co.
N/A