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S. Lawson
M. Lisa Battista
D. Blaise
E. Calore
S. Cesaro
N. Maximova
K. Perruccio
R. Wynn
M. Zecca
M. Labopin
V. Amber
R. J. Ryan
M. Mohty
Birmingham Children's Hospital, Birmingham, United Kingdom
Rheumatology Clinic, University of Udine, Udine, Italy
Institut Paoli-Calmettes, Marseille, France
The Clinic of Pediatric Hematology–Oncology, University Hospital of Padova, Padua, Italy
Pediatric Hematology‐Oncology, “Ospedale della Donna e del Bambino”, Verona
Institute for Maternal and Child Health IRCCS Burlo Garofolo, Trieste, Italy
Pediatric Oncology and Hematology Section, Santa Maria della Misericordia Hospital, Perugia, Italy,
Royal Manchester Children's Hospital, Manchester, United Kingdom
Paediatric Haematology / Oncology, Fondazione IRCCS, Policlinico San Matteo Foundation, Pavia, Italy,
Hôpital St Antoine, Sorbonne University, INSERM UMRs 938, Paris, France
Jazz Pharmaceuticals, Oxford
Jazz Pharmaceuticals, Inc., Philadelphia, PA
United Kingdom
Italy
France
United States
N/A
Gastroenterology (GU)
Hepatic veno-occlusive disease with immunodeficiency
Hematocrit
Defibrotide
N/A
Observational
Multinational
Multicenteric
Prospective
NA
NCT03032016
N/A
N/A