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BSH2020‐PO‐037 : Patients’ and health care professionals’ perspectives on treatment goals in sickle cell disease – a UK perspective: results from the International Sickle Cell World Assessment Survey (SWAY)

Researchers

Presenter

  • B. Inusa

Principal Investigators

  • J. James

  • O. Rajkovic-Hooley

  • T. Bailey

  • G. Medalla

  • B. Taylor

Medical Centers

  • Paediatric Haematology, Evelina Children's Hospital,Guy's and St Thomas' Hospital,London,Royaume-uni

  • Sickle Cell Society

  • Adelphi Real World, London

  • Adelphi Real-World, Bollington, UK

  • BioMarin Pharmaceuticals, London, UK

Locations

  • United Kingdom

Companies

  • N/A

Study Components

Therapeutic Area

  • Musculoskeletal

  • Blood/haematological Diseases

Disease

  • Sickle cell anemia

  • Chronic pain

Biomarkers

  • Alpha-1-microglobulin/bikunin precursor

  • Stearoyl-CoA desaturase

  • Volatile organic compounds

Drug/Treatment

  • N/A

Outcome

  • N/A


Study Design

  • Multinational

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • N/A

Result

  • N/A