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P151 : Effectiveness and Safety of rFVIIA in Paediatric Glanzmann Thrombasthenia Patients: Data From the International Glanzmann Thrombasthenia Registry

Researchers

Presenter

  • R. Zotz

Principal Investigators

  • M.-C. Poon

  • G. Di Minno

  • N. Bindslev

  • R. D'Oiron

Medical Centers

  • Center for Laboratory Medicine, Blood Coagulation and Transfusion Medicine (LBT), Düsseldorf, Germany

  • Departments of Medicine, Pediatrics and Oncology, University of Calgary Foothills Hospital, Calgary, AB, Canada

  • Department of Clinical Medicine and Surgery, Regional Reference Center for Coagulation Disorders, Federico II University, Naples, Naples, Italy

  • Biostatistics, Novo Nordisk A/S, Søborg, Denmark

  • Centre for Hemophilia and Rare Congenital Bleeding Disorders, University Hospitals, Paris‐Sud, AP‐HP, Bicêtre Hospital, Le Kremlin‐Bicêtre, France

Locations

  • Germany

  • Canada

  • Italy

  • Denmark

  • France

Companies

  • N/A

Study Components

Therapeutic Area

  • Blood/haematological Diseases

  • Genetic Disorder

Disease

  • N/A

Biomarkers

  • N/A

Drug/Treatment

  • rFVIIa

Outcome

  • N/A


Study Design

  • Observational

  • Multinational

  • Multicenteric

Phase

  • NA

Study Id's

  • N/A

Sponsors

  • CSL Behring

Result

  • N/A