//
You-Hai Xu
Gregory A Grabowski
Hong Du
Gordon A Francis
Cincinnati Children's Hospital, Cincinnati, OH
IN Univ Sch of Med, Indianapolis, IN
The University of British Columbia, Vancouver, BC, Canada
United States
Canada
N/A
Genetic Disorder
Endocrine/metabolic Diseases (ME)
Lysosomal acid lipase deficiency
Niemann-Pick disease type C
Coronary Artery Disease
Cholesterol
lipase
N/A
N/A
NA
N/A
N/A
Interim