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Katherine L Madson
Michael P Whyte
Marisa Gayron
Kenji Fujita
Cheryl Rockman-Greenberg
Shriners Hosp for Children, Saint Louis, MO
Duke University Medical Center, Durham, NC
United States
Canada
Alexion Pharmaceutic
Genetic Disorder
Hypophosphatasia
Alkaline phosphatase
Alkaline Phosphatase, Biomineralization Associated
Myelin proteolipid protein
Alkaline phosphatase
Strensiq
N/A
open label
randomized
NA
N/A
N/A
Interim